Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 (SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA) | Journal of Medicinal Chemistry
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Biogen on Twitter: "#SMA is caused by a mutation in the survival motor neuron 1 (SMN1) gene, which maintains the health and normal function of motor neurons. https://t.co/uUdVjujm9P" / Twitter
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The Function of Survival Motor Neuron Complex and Its Role in Spinal Muscular Atrophy Pathogenesis - ScienceDirect
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JCM | Free Full-Text | New Treatments in Spinal Muscular Atrophy: Positive Results and New Challenges
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Survival motor neuron function and spinal muscular atrophy pathology.... | Download Scientific Diagram
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Spinal muscular atrophy: why do low levels of survival motor neuron protein make motor neurons sick? | Nature Reviews Neuroscience
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Queen Mary Hospital and The Duchess of Kent Children's Hospital at Sandy Bay, Hong Kong<br>Paediatric Neuromuscular Diagnostic and Management Program
P. D. Hinduja Hospital - Spinal Muscular Atrophy (SMA) is caused due to absence of survival motor neuron 1 gene. It causes difficulties to stand, walk, control head movements, and in some
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Spinal Muscular Atrophy: A Deficiency in a Ubiquitous Protein; a Motor Neuron-Specific Disease: Neuron
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Survival Motor Neuron Protein in Motor Neurons Determines Synaptic Integrity in Spinal Muscular Atrophy | Journal of Neuroscience
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Interferons and IRF-1 Induce Expression of the Survival Motor Neuron (SMN) Genes | Molecular Medicine | Full Text
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